Is gene therapy research for single-gene diseases at risk under Trumpcare? – Genetic Literacy Project
Genetic Literacy Project |
Is gene therapy research for single-gene diseases at risk under Trumpcare?
Genetic Literacy Project The high cost of lifelong frequent infusions or injections of ERT is why the “forever fix” of a gene therapy is an attractive alternative, even if a booster or two becomes necessary. Gene therapy delivers the DNA instructions for making the missing enzyme. |
