New gene therapy trial for X-linked myotubular myopathy offers hope to children – News-Medical.net
News-Medical.net |
New gene therapy trial for X-linked myotubular myopathy offers hope to children
News-Medical.net Ann & Robert H. Lurie Children's Hospital of Chicago is one of the few centers participating in ASPIRO, an international Phase 1/2 clinical trial of a gene therapy product called AT132 for X-linked myotubular myopathy – a rare disease characterized by … |
