Sanfilippo syndrome gene therapy could be filed in US next year, Abeona – BioPharma-Reporter.com
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Sanfilippo syndrome gene therapy could be filed in US next year, Abeona
BioPharma-Reporter.com But while pharma firms such as Shire, Alexion and BioMarin are investigating enzyme replacement therapies, Abeona says its gene therapy candidate ABO-102 could offer patients a cure delivered by a single injection. In February, Abeona presented … |
