SMA Gene Therapy Promising in Early Results – MedPage Today
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SMA Gene Therapy Promising in Early Results
MedPage Today BOSTON — Early results from a small phase I trial of a gene therapy for spinal muscular atrophy (SMA) were promising, with many children hitting milestones not typically seen in the condition, researchers said here. In the latest update from the trial … Gene Therapy Found to Benefit Infants with SMA in Small Open-Label Study |
