FierceBiotechGold nanoparticles effectively deliver CRISPR to mouse models of DMDFierceBiotechThe three components of CRISPR—the Cas9 enzyme, a guide RNA and donor DNA—are delivered using a viral vector, most commonly an adeno-associated virus (AAV). … Continue reading
Phys.OrgNew CRISPR tool targets RNA in mammalian cellsPhys.OrgResearchers from the Broad Institute of MIT and Harvard have shown that a CRISPR-based editing system can cut and bind RNA in mammalian cells. In a paper out this week in Nature, the team us… Continue reading
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Facebook billionaires Peter Thiel and Sean Parker backing a stealth immunotherapy biotech — report
Endpoints News And they are working on cancer immunotherapies, the hottest field in the R&D arena these days. Garcia — a high profile investigator — has been working on Wnt, noting that an excess of activity triggers cancer. Earlier this year a startup dubbed … |
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Poseida Therapeutics Presents Preclinical Solid Tumor Data for P-PSMA-101, a CAR–T Therapy Predominantly …
GlobeNewswire (press release) SAN DIEGO, Oct. 05, 2017 (GLOBE NEWSWIRE) — Poseida Therapeutics Inc. (“Poseida”), a San Diego-based clinical-stage company translating best-in-class gene therapy technologies into lifesaving cell therapies, today presented preclinical data on … |
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WindMIL Therapeutics Announces New Cancer Immunotherapy Approach Based on Marrow-Infiltrating Lymphocytes
Business Wire (press release) BALTIMORE–(BUSINESS WIRE)–WindMIL Therapeutics, a clinical stage company developing Marrow-Infiltrating Lymphocytes (MILs™) for cancer immunotherapy, today presented its novel approach to harnessing a patient’s immune system to treat solid … |
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Bluebird’s gene therapy shows promise in keeping lethal Lorenzo’s Oil disease in check
Endpoints News After an average of 29 months following a one-time gene therapy infusion, a clear majority of boys suffering from lethal cases of cerebral adrenoleukodystrophy were alive and free of major complications from the disease — the primary endpoint in the … |