News & ObserverGene therapy company bringing 200 jobs to DurhamNews & ObserverAveXis, a clinical-stage gene therapy company that makes treatments for spinal muscular atrophy, plans to create 200 jobs in Durham County, after receiving an incentive packa… Continue reading
OncLiveNovel Immunotherapy Shows Early Efficacy in Uveal MelanomaOncLiveIMCgp100, a novel immune-based treatment, demonstrated a 1-year survival rate of 73% (95% CI, 46%-88%) for patients with heavily pretreated, advanced uveal melanoma, which is nearl… Continue reading
Investor’s Business DailyMomentum grows for hemophilia gene therapies | BioPharma DiveBioPharma DiveAn experimental gene therapy developed by BioMarin Pharmaceutical eliminated spontaneous bleeding and restored activity of a blood clotting protein to&n… Continue reading
TimeGazetteSynthetic Biology Market 2025 with Focus on Emerging Technologies, Global Trends, Competitive Landscape …Expert ConsultingSynthetic Biology Market – Global Market Synopsis, Growth Factors, Industry Segmentation, Regional Analysis And Compe… Continue reading
Business Wire (press release)T-Cell Immunotherapy Market Projected to Grow at an Annualized Rate of 86%, Predicts Roots AnalysisBusiness Wire (press release)Pemba Lahmo, the principal analyst, stated, “With two approved therapies and over 480 clinical… Continue reading
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Trial Results Are Positive For Two Rare Disease Gene Therapies
Pharmaceutical Processing To date, 11 patients have been dosed with a single intravenous injection of the ABO-102 gene therapy for systemic delivery of a functional copy of the missing SGSH gene associated with onset and progression of the disease. The SGSH gene provides … Explore the latest developments in ATMPs at SMi’s Cell & Gene Therapy 2018EIN News (press release) |
FierceBiotech |
Spark hemophilia B gene therapy clears test en route to Pfizer …
FierceBiotech Spark Therapeutics has presented data on hemophilia B patients who received a version of its gene therapy manufactured using a modified process. Early data … Hunting a cure, Spark reports steady progress on hemophilia B …Endpoints News Spark’s gene therapy SPK-9001 shows treatment benefit in …Seeking Alpha Spark, Pfizer report progress on gene therapy for hemophiliaPhiladelphia Business Journal pharmaphorum –PMLiVE all 27 news articles » |