Trial Results Are Positive For Two Rare Disease Gene Therapies – Pharmaceutical Processing
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Trial Results Are Positive For Two Rare Disease Gene Therapies
Pharmaceutical Processing To date, 11 patients have been dosed with a single intravenous injection of the ABO-102 gene therapy for systemic delivery of a functional copy of the missing SGSH gene associated with onset and progression of the disease. The SGSH gene provides … Explore the latest developments in ATMPs at SMi's Cell & Gene Therapy 2018 |
