U. of Missouri-led scientists improve gene transfer in Duchenne therapy – FierceBiotech
FierceBiotech |
U. of Missouri-led scientists improve gene transfer in Duchenne therapy
FierceBiotech Gene therapy seeks to treat DMD by restoring dystrophin production. Adeno-associated viruses (AAV) are used to deliver the gene, as they do not cause disease in humans. But because the dystrophin gene is too large for the virus to carry, researchers … |
