Young Boy Becomes First DMD Patient to Receive Investigational Systemic Microdystrophin Gene Therapy – Muscular Dystrophy News
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Young Boy Becomes First DMD Patient to Receive Investigational Systemic Microdystrophin Gene Therapy
Muscular Dystrophy News The first Duchenne muscular dystrophy (DMD) patient has received systemic microdystrophin gene therapy as part of a Phase 1/2 clinical trial at Nationwide Children's Hospital in Columbus, Ohio. The trial (NCT03375164), currently recruiting participants … |
